Rare Diseases Day: targeting unknown diseases in children

The children’s charity Action Medical Research marked the annual global Rare Diseases Day on 28 February 2014 by announcing vital research breakthroughs and continuing investment into diseases for which there are often no cures. The charity aims to make a difference through medical research by tackling premature birth, treating sick and vulnerable babies, helping children affected by disability, disabling conditions and infections, and targeting rare diseases that together affect many children. Research is the key to saving many of these children from a lifetime of suffering and Action Medical Research is currently funding more than 14 different studies targeting rare diseases.